This clinical study is sponsored by Neuren Pharmaceuticals, a biopharmaceutical company headquartered in Melbourne, Australia focusing on the development of therapies for neurodevelopmental and neurodegenerative disorders. Current trials target neurodevelopmental disorders such as Pitt Hopkins, Angelman, and Phelan-McDermid syndromes.

For more information on these upcoming studies, please visit

For more information on Neuren Pharmaceuticals, visit

Further information provided by other websites and organizations for additional resources about Pitt Hopkins syndrome can be found below.

PHRF (Pitt Hopkins Research Foundation)

PHRF has a mission to support research dedicated to finding a treatment, and an eventual cure for Pitt Hopkins syndrome and other similar disorders. PHRF is also dedicated to supporting the Pitt Hopkins community with resource recommendations, parental support, and the latest medical information.

More information can be found at is a registry and results database of publicly and privately supported clinical studies of human participants conducted around the world, according to their website. The service is supported by the National Institutes of Health.
You can find our entry at:

Reimbursement Information

PHRF will administer funds to support families for their participation in this Pitt Hopkins syndrome study.

If you are interested in receiving travel support towards participation in the study, or would like further information, please contact the PHRF directly via email at .

In order to ensure that we’re able to support future families in this trial, it may not be possible to approve 100% of your estimated expenses, but we will do our best to meet your needs. Thank you for your understanding and dedication to advancing research for Pitt Hopkins Syndrome.